Publications

Tobias B. Polak, David G J Cucchi, Jasmin Schelhaas, Syed S Ahmed, Naima Khoshnaw, Joost van Rosmalen, Carin A Uyl-de Groot (2023). Results from Expanded Access Programs: A Review of Academic Literature.

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Tobias B. Polak, David G. J. Cucchi, Jasmin Schelhaas, Syed S. Ahmed, Naima Khoshnaw, Joost van Rosmalen, Carin A. Uyl – de Groot (2023). Results from Expanded Access Programs: A Review of Academic Literature. Drugs.

Tobias Boy Polak, Holly Fernandez Lynch (2023). The Ethics of Expanded Access Research. JAMA.

Tobias B Polak, David G J Cucchi, Joost van Rosmalen, Carin A Uyl-de Groot (2022). The DRUG Access Protocol: Access Inequality and European Harmonisation. The Lancet Oncology.

Tobias B. Polak, David G. J. Cucchi, Joost van Rosmalen, Carin A. Uyl – de Groot, Jonathan J. Darrow (2022). Generating Evidence from Expanded Access Use of Rare Disease Medicines: Challenges and Recommendations. Frontiers in Pharmacology.

Tobias B Polak, David GJ Cucchi, Jonathan J Darrow, Matthijs M Versteegh (2022). Incremental Benefits of Novel Pharmaceuticals in the UK: A Cross-Sectional Analysis of NICE Technology Appraisals from 2010 to 2020. BMJ Open.

David GJ J. Cucchi, Tobias B. Polak, Gert J. Ossenkoppele, Jacob M. Rowe, Elihu H. Estey (2022). The Predictive Value of a Positive Phase II ASH Abstract for Peer-Reviewed Publication and Progression to Phase III. Blood.

Tobias B Polak, David GJ Cucchi, Joost van Rosmalen, Carin A Uyl-de Groot (2022). Real-World Data from Expanded Access Programmes in Health Technology Assessments: A Review of NICE Technology Appraisals. BMJ Open.

Carolien Duetz, David G. J. Cucchi, Tobias B. Polak, Jeroen J. W. M. Janssen, Gert J. Ossenkoppele, Elihu H. Estey, Arjan A. Loosdrecht (2021). The Wider Perspective: Twenty Years of Clinical Trials in Myelodysplastic Syndromes. British Journal of Haematology.

Tobias B. Polak, Eline M. Bunnik (2021). Financial Considerations in Expanded Access Policy for Gene Therapies: A Tough Nut to Crack?. Molecular Therapy.

David G. J. Cucchi, Tobias B. Polak, Gert J. Ossenkoppele, Carin A. Uyl–De Groot, Jacqueline Cloos, Sonja Zweegman, Jeroen J. W. M. Janssen (2021). Two Decades of Targeted Therapies in Acute Myeloid Leukemia. Leukemia.

Tobias B Polak, David G J Cucchi, Joost van Rosmalen (2021). [Expanded Access in The Netherlands: prescribing unregistered medicine].. Nederlands tijdschrift voor geneeskunde.

Tobias B Polak, Joost van Rosmalen, Carin A. Uyl – de Groot, Carin A Uyl-de Groot (2020). Response to Open Peer Commentary \"Making It Count: Extracting Real World Data from Compassionate Use and Expanded Access Programs\".. The American journal of bioethics : AJOB.

Tobias B. Polak, Joost van Rosmalen, Joost Rosmalen, Carin A. Uyl – de Groot (2020). Expanded Access as a Source of Real-World Data: An Overview of FDA and EMA Approvals. British Journal of Clinical Pharmacology.

T. Polak, C.A. Uyl-de Groot, J. Van Rosmalen (2019). PNS410 DATA FROM EXPANDED ACCESS PROGRAMS: TREATMENT FIRST, COLLECTION SECOND. AN OVERVIEW OF FDA AND EMA REGULATORY APPROVALS.. Value in Health.

Tobias Polak (2019). An example preprint / working paper.

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Tobias Polak, Robert Ford (2015). An example journal article. Journal of Source Themes, 1(1).

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